Long-term expression of FVIII:C following AAV-FVIII with improvement in global hemostatic profiles. CSAFVIII, chromogenic substrate assay FVIII; OSAFVIII, one-stage assay FVIII; WBCT, normal range: 2-6 minutes. ∗Nonresponder.
Figure 2.

Long-term expression of FVIII:C following AAV-FVIII with improvement in global hemostatic profiles. CSAFVIII, chromogenic substrate assay FVIII; OSAFVIII, one-stage assay FVIII; WBCT, normal range: 2-6 minutes. ∗Nonresponder.

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