Best response and follow-up in BPDCN
| Subject number . | Dose/schedule . | Cause for treatment interruption or lack of completion . | Overall response . | Length of response (months) . | Cause of death . |
|---|---|---|---|---|---|
| 1 | Five consecutive daily doses | CR | 5 | See 1B | |
| 1B | Five consecutive daily doses | PD | — | Progressive disease | |
| 2 | Three consecutive daily doses | Low albumin + DVT | CR | 20+ | Alive in remission |
| 3 | Two consecutive daily doses; then 3 consecutive daily doses 1 week later | ALT elevation | PD | — | Alive with progressive disease |
| 4 | Five consecutive daily doses | PD | — | Progressive disease | |
| 5 | Five consecutive daily doses | CR | 3 | See 5B | |
| 5B | Five consecutive daily doses | PD | — | Progressive disease + advanced RCC | |
| 6 | Five consecutive daily doses | CR | 3+ | Alive in remission | |
| 7 | Five doses over 6 days | ALT elevation | CR | 7+ | Alive in remission |
| 8 | One dose | Creatinine elevation | PR | 1 | See 8B |
| 8B | Two consecutive daily doses | Creatinine elevation | PD | — | Alive with progressive disease |
| 9 | Two consecutive daily doses | ALT elevation | NE | — | Alive with progressive disease |
| 10 | Five consecutive daily doses | PR | 4+ | Alive with partial remission | |
| 11 | One dose | Clinical deterioration possibly due to BPDCN | NE | — | Presumed progressive disease |
| Subject number . | Dose/schedule . | Cause for treatment interruption or lack of completion . | Overall response . | Length of response (months) . | Cause of death . |
|---|---|---|---|---|---|
| 1 | Five consecutive daily doses | CR | 5 | See 1B | |
| 1B | Five consecutive daily doses | PD | — | Progressive disease | |
| 2 | Three consecutive daily doses | Low albumin + DVT | CR | 20+ | Alive in remission |
| 3 | Two consecutive daily doses; then 3 consecutive daily doses 1 week later | ALT elevation | PD | — | Alive with progressive disease |
| 4 | Five consecutive daily doses | PD | — | Progressive disease | |
| 5 | Five consecutive daily doses | CR | 3 | See 5B | |
| 5B | Five consecutive daily doses | PD | — | Progressive disease + advanced RCC | |
| 6 | Five consecutive daily doses | CR | 3+ | Alive in remission | |
| 7 | Five doses over 6 days | ALT elevation | CR | 7+ | Alive in remission |
| 8 | One dose | Creatinine elevation | PR | 1 | See 8B |
| 8B | Two consecutive daily doses | Creatinine elevation | PD | — | Alive with progressive disease |
| 9 | Two consecutive daily doses | ALT elevation | NE | — | Alive with progressive disease |
| 10 | Five consecutive daily doses | PR | 4+ | Alive with partial remission | |
| 11 | One dose | Clinical deterioration possibly due to BPDCN | NE | — | Presumed progressive disease |
B, second course; NE, not evaluable as withdrew consent; DVT, deep vein thrombosis.